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Cruz, Lilian and Bence, György and Cheah, Pike See and Kleinstiver, Benjamin P. and Eimer, William A. and Garcia, Sara P. and Sharma, Nutan and Ozelius, Laurie J. and Cristopher, Bragg D. and Joung, Keith J. and Norberto de Souza, Osmar and Macedo Timmers, Luis Fernando Saraiva and Breakefield, Xandra O. (2020) Mutant allele-specific CRISPR disruption in DYT1 dystonia fibroblasts restores cell function. Molecular Therapy-Nucleic Acids, 21. pp. 1-12. ISSN 2162-2531